• HotSpot Therapeutics Secures $45M to Advance Drug Discovery Platform
  • Cerebrospinal Fluid Biomarker NfL Can Help Monitor Nerve Cell Degeneration, Study Says
  • NeuroVive Licenses BridgeBio Subsidiary to Develop LHON Therapies
  • Older Moms More Likely to Pass Along Mitochondrial DNA with Mutations, Study Finds
  • Stealth Raises $100M to Advance Elamipretide as Treatment for Mitochondrial Diseases
  • Mutations in Mitochondrial Gene ANT1 Linked to Risk of Bipolar Disease in Mouse Study
  • Mutations in MRPS2 Gene Linked to Mitochondrial Dysfunction for First Time, Case Report Shows
  • US ‘Right to Try’ Law Meets with Mix of Praise and Criticism, Including Among Those with Rare Diseases
  • Surveys Details Reasons Mitochondrial Disease Patients Take Part – or Don’t – in Clinical Trials
  • #ERDC2018 – When Treating Rare Disease Patients, Don’t Overlook Quality of Life, Panel Urges
  • Phase 1 Clinical Trial Testing Potential Mitochondrial Disease Therapy KL1333 Shows Positive Results
  • Mitochondrial Disease Treatment Candidate KH176 Shows Potential, Study Finds